Meetings

Children’s National Hospital at the 2026 Pediatric Academic Societies meeting

PAS 2026 logoExperts affiliated with Children’s National Hospital will attend the 97th Pediatric Academic Societies (PAS) Meeting, taking place in Boston from April 24-27, 2026. For details on presentations by Children’s National, please see the chart below and visit the PAS agenda page.

 

Date/Time Main Presenter(s) Presentation Title
April 24
12:30-2:00 p.m.
Melissa Meyers Personalized Immunosuppression in Pediatric Kidney Transplant Recipients
April 24
4:00-5:30 p.m.
Elizabeth Hubbard Stand Out in Seconds: Develop Your Personal Brand, Elevator Pitch, and Interview Skills
April 24
4:00-5:30 p.m.
Tamara L. Gayle Hospital Medicine | Innovation in PHM: Digital Tools and AI Breakthroughs and Missteps
April 24
4:00-5:30 p.m.
Dewesh Agrawal Emergency Medicine 1
April 24
4:15-4:30 p.m.
Celina Brunson How High is Too High? Severe Hyperparathyroidism and bone mineral disease in children on hemodialysis
April 24
4:45-5:00 p.m.
Muhammad M. Rahman Machine Learning to Predict 30-day Emergency Department Revisit Among Youth with Mental or Behavioral Health Concerns
April 24
5:30-8:00 p.m.
Yao Wu Associations Between Maternal Mental Health and Amygdala and Hippocampus Volumes in Newborns with Antenatal Opioid Exposure
April 24
5:30-8:00 p.m.
Alicia Rolin Availability and Knowledge of Naloxone Distribution in an Urban Area
April 24
5:30-8:00 p.m.
Olivia Gould Barriers and Enablers to Pediatric Donation after Cardiac Death (DCD): A Qualitative PICU Study
April 24
5:30-8:00 p.m.
Margaret Rush Blood Culture Utilization for Children with High Intensity Neurological Impairment Hospitalized for Pneumonia
April 24
5:30-8:00 p.m.
William Gravley Electrical Impedance Tomography to Monitor Lung Inflation in Bronchopulmonary Dysplasia: A Feasibility Study
April 24
5:30-8:00 p.m.
Megan L. Smith Evaluation of Associations among Food Insecurity Severity, Public Benefit Use, and Pediatric Asthma Outcomes
April 24
5:30-8:00 p.m.
Christopher Gable Factors Associated with Emergency Holds in Acute Pediatric Mental and Behavioral Health Presentations
April 24
5:30-8:00 p.m.
Jordy Salcedo-Giraldo Graphic Novels for Pediatric Hypertension: Enhancing Health Literacy and Medication Adherence through Visual Storytelling
April 24
5:30-8:00 p.m.
Thevaa Chandereng Mental Health Newborn Screening: False Positive Rates and Temperature Data Insights
April 24
5:30-8:00 p.m.
Jasmine Preston Turner Parental Perceptions of Mental Health and Utility of Mental Health Resources Provided in PICU Admissions
April 25
8:00-9:30 a.m.
Kevin Lloyd, Jacqueline Saito Prescribing with Purpose: The Role of Stewardship in All Pediatric Fields
April 25
9:00-9:10 a.m.
Nathan Kuppermann Planning and Execution of a Large Pragmatic Multinational Emergency Care Trial in Children
April 25
11:00 a.m.-12:30 p.m.
Padmaja Pavuluri Beyond the Grid: Smarter Scheduling, Stronger Teams, and World Peace
April 25
11:00 a.m.-12:30 p.m.
Sadiqa Kendi When a Meal Train is Not Enough: Tools for Supporting Academic Pediatricians Experiencing Serious Illness
April 25
2:00-3:30 p.m.
Ilana Lavina Beyond Discharge: Practicing Safety Planning for Youth at Risk for Suicide Across Pediatric Settings
April 25
11:00 a.m.-12:30 p.m.
Monika Goyal Health Equity/Social Determinants of Health 2
April 25
2:00-3:30 p.m.
Sarah B. Mulkey Global Neonatal & Children’s Health 1
April 25
2:45-3:00 p.m.
Andrea Hahn Virus Prevalence in Children with Tracheostomy and Home Ventilation during Health and Acute Respiratory Infection and Relation of Virus Detection to ARI Severity
April 25
3:30-5:45 p.m.
Sudeepta Basu Active Sleep During Extrauterine Third Trimester is Associated with Neurophysiologic Maturation in Preterm Infants
April 25
3:30-5:45 p.m.
Sudeepta Basu Active Sleep During Extrauterine Third Trimester is Positively Associated with Brain White Matter Volume in Preterm Infants
April 25
3:30-5:45 p.m.
Youness Arjoune AI-Enabled Auto Capture of Throat Images for Smartphone-Based Oropharyngeal Examination in Pediatric Patients
April 25
3:30-5:45 p.m.
Adenike Animasaun Caregiver Perspectives on School Asthma Management Post Exacerbation: A Qualitative Study
April 25
3:30-5:45 p.m.
Emese Kanyo Characterizing Hospital-Based Provision of Longitudinal Asthma Care in Children ≤ 4 Years Old
April 25
3:30-5:45 p.m.
Manuela Iglesias Diferencias en el neurodesarrollo infantil temprano tras la infección materna sintomática y asintomática por SARS-CoV-2 durante el embarazo
April 25
3:30-5:45 p.m.
Kelly Christensen Feasibility, Recruitment, and Retention of a Multi-State, Longitudinal Study of Parents’ Newborn Screening Experiences
April 25
3:30-5:45 p.m.
Maria Triantafyllou Human Mesenchymal Stem Cell Derived Extracellular Vesicles Attenuate Sepsis-Induced Acute Lung Injury via Immune Modulation
April 25
3:30-5:45 p.m.
Simranjeet S. Sran Improving Medical Student Physical Diagnosis and Diagnostic Reasoning Skills in a Pre-Clinical Doctoring Course
April 25
3:30-5:45 p.m.
Allen Yiu Investigating the Association Between Healthcare Contact and Chronic School Absenteeism: Insights from Integrated Clinical and Educational Data
April 25
3:30-5:45 p.m.
Yao Wu Neonatal Brain Volumes Differ Across Neurobehavioral Profiles and Vary by Antenatal Opioid Exposure
April 25
3:30-5:45 p.m.
Jung-Hoon Kim Nonlinear Brain Network Disruption in Opioid-Exposed Neonates Revealed by Deep Generative Modeling
April 25
3:30-5:45 p.m.
Allen Yiu Pediatric Primary Care Providers’ Perspectives on Accessing and Using School-Based Information: A Mixed-Methods Exploration
April 25
3:30-5:45 p.m.
Anola Stage Relationship of Clinical Co-morbidities with the Altered Maturational Trajectory of Cerebral Metabolites in Preterm Infants
April 25
3:30-5:45 p.m.
Josepheen De Asis-Cruz The Newborn Connectome in Antenatal Opioid Exposure
April 25
3:30-5:45 p.m.
Brittany N. Fitzpatrick Walking Towards Equity: Enhancing Pediatric Pedestrian Safety Through Data Driven Solutions
April 26
8:00-9:30 a.m.
Dewesh Agrawal Emergency Medicine 4
April 26
8:00-9:30 a.m.
Alicia Tucker Nutrition and Food is Medicine and Obesity Combined SIG | Navigating Nutrition Counseling and Resources for Patients Experiencing Food and Nutrition Insecurity
April 26
8:00-9:30 a.m.
Alexandra Corley Publishing Partners: Cultivating the mentorship relationship for a successful publication process
April 26
8:15-8:30 a.m.
Rana F. Hamdy StrepApp: A Machine Learning-Based Tool for Diagnosing GAS Pharyngitis in Children
April 26
8:15-8:45 a.m.
Susan Walley Oops, Tobacco Companies Did It Again!: New Tobacco and Nicotine Products Addicting Youth
April 26
8:30-8:45 a.m.
Nora Wolff Sepsis Causes a Region-Specific Pattern of Metabolic Dysfunction in the Murine Brain
April 26
9:30-11:30 a.m.
Rachael Odusanya Exploring Outcomes of the DC Health and Academic Prep Program (DC HAPP) at the George Washington University School of Medicine and Health Sciences: A Qualitative Evaluation
April 26
9:30-11:30 a.m.
Shilpa J. Patel Facilitating Housing Intervention Uptake in Pediatric Asthma: The Role of Screening Checklists and Medical Interviews
April 26
9:30-11:30 a.m.
Tamara L. Gayle Feeding Engagement, A Food Insecurity Curriculum
April 26
9:30-11:30 a.m.
Srikanth R. Damera Fetal Brain Shape Predicts Gestational Age and Early Dysmaturation in Congenital Heart Disease
April 26
9:30-11:30 a.m.
Caroline Wambach Social-Emotional Development and Functional Connectivity in Neonates
April 26
9:30-11:30 a.m.
Jessica Weisz “TEACH”ing Advocacy: Assessment of trainee advocacy messages with an evidence-based assessment tool
April 26
9:30-11:30 a.m.
Bridget Allard Trends of Observation Stays at Children’s Hospitals (2019-2024)
April 26
9:30-11:30 a.m.
Shilpa J. Patel Quality Improvement and Equity: A Multisite Study of Disparities in Pediatric Mental Health Interventions
April 26
11:00 a.m.-1:00 p.m.
Nimisha Bajaj Finding Connection Through Reflective Practice: Tools for Weaving Narrative Medicine Into the Workplace
April 26
11:30 a.m.-1:00 p.m.
Lenore Jarvis Empowering Pediatricians: Resilience and Risk Strategies for Effective Advocacy
April 26
12:20-12:45 p.m.
Tammy Brady Measuring What Matters: Evaluating Implementation Outcomes in Pediatric Hypertension Initiatives
April 26
12:30-12:45 p.m.
Josepheen De Asis-Cruz Altered Hypothalamic Structure and Functional Connectivity in Neonates Exposed to Maternal Diabetes
April 26
12:40-1:00 p.m.
Annie Andrews Equity, Identity, and Peer Support In Advocacy Spaces
April 26
2:30-4:00 p.m.
Kevin M. Cook Neonatal Neurology 4: Clinical – Prenatal
April 26
2:30-2:45 p.m.
Katherine Ottolini Impaired Ex Utero Brain Growth of Preterm Infants compared to In Utero Healthy Fetuses
April 26
2:30-4:00 p.m.
Christina Lindgren Simulation-based Medical Education (SBME)
April 26
2:45-3:00 p.m.
Kevin M. Cook Maturation of Functional Brain Connectivity in Preterm Infants Differs from Fetal Development and Based on Age at Birth
April 26
2:45-3:10 p.m.
Nathan Kuppermann Federal Funding in the Current Landscape
April 26
3:45-4:00 p.m.
Sarah B. Mulkey Normocephalic Colombian Children with Antenatal Zika Virus Exposure Have Differences in Neurodevelopmental Trajectories and on Brain MRI at 7 Years of Age
April 26
3:35-4:00 p.m.
Monika Goyal Grant Termination and Pivot To Other Financial Sources
April 27
8:00-10:00 a.m.
Jessica M. Hippolyte Assessing Racial and Ethnic Disparities in Pediatric Prehospital Pain Management
April 27
8:00-10:00 a.m.
Elizabeth Ireson Civic Engagement for a Healthier Tomorrow: Voter Registration in a Large Pediatric Healthcare System
April 27
8:00-10:00 a.m.
Jessica Weisz Characteristics and Medical Needs of Uninsured Pediatric Immigrant Patients Referred to Care Coordination Program Based at an Academic Tertiary Care Hospital
April 27
8:00-10:00 a.m.
Nora Wolff Cross-Species Biomarkers of Cerebellar Injury In Acute Sepsis: Integrated Metabolomics of Mouse Cerebellum and Plasma Identify Conserved Human Plasma Biomarkers and Therapeutic Modulation by MSC-sEVs
April 27
8:00-10:00 a.m.
Ashley V. Trinh Examining the Association Between Normalized Protein Catabolic Rate and Bone Disease in Pediatric Patients on Chronic Hemodialysis
April 27
8:00-10:00 a.m.
Theodore E. Trigylidas Improving Patient and Caregiver Experience at a Pediatric Emergency Department
April 27
8:00-10:00 a.m.
Anola Stage Improving Vaccination Rates in a Level IV NICU
April 27
8:00-10:00 a.m.
Gabrielle Jasmin Incidence of Bacteremia in Patients with Fever and Sickle Cell Disease Who Present to the Emergency Department
April 27
8:00-10:00 a.m.
Elan L. Donnellan Neurobehavioral Stress Linked to the Central Nervous System is Associated with Heart Rate Variability Differences in Preterm Infants
April 27
8:00-10:00 a.m.
Lauretta A. Oseni Parent Health Literacy and Medication Comprehension for Children with Medical Complexity
April 27
8:00-10:00 a.m.
Maneesha Sakhuja Patterns in Clinical Ethics Consultations in Hospitalized Children with Medical Complexity
April 27
8:00-10:00 a.m.
Laura O’Neill Problem- vs. Systems-Based Clinical Documentation on Measures of Clinical Reasoning, Diagnostic Accuracy, and Mental Demand Among Residents
April 27
8:00-10:00 a.m.
Shireen M. Atabaki School Based Telehealth Access and Resources for Mental Health Care for Students
April 27
8:00-10:00 a.m.
Nimisha Bajaj Simulation-Based Approach to Emergencies in Pediatric Comfort Care
April 27
8:00-10:00 a.m.
Molly Schneider The Epidemiology and Clinical Presentation of Pediatric Sepsis in the Prehospital Setting
April 27
8:00-10:00 a.m.
Gabriele Simonti Timing and Intensity of Sensory-Motor Therapies Shapes Cerebellar-Mediated Motor and Social Outcomes After Prematurity-Related Insults
April 27
10:00-11:30 a.m.
Susan Walley Vapes, Nicotine Pouches, and Cigarettes: New Clinical Guidelines for Treatment of Adolescent Nicotine and Tobacco Use
April 27
10:00-10:15 a.m.
Megan Prior Evaluating a Medical-Educational Advocate Partnership: A Retrospective Analysis of Referral Demographics and Stakeholder Satisfaction
April 27
10:00-10:15 a.m.
Shilpa J. Patel Improving Mental Health Processes, Workflows, and Responses Quality Collaborative
April 27
10:15-10:30 a.m.
Srikanth R. Damera Fetal Subplate Dysmaturation Predicts Early Motor Outcomes in Congenital Heart Disease
April 27
10:30-10:50 a.m.
Susan Walley Landscape of New Tobacco and Nicotine Products
April 27
11:00-11:15 a.m.
Alicia Rolin Impact of an EHR-Embedded Clinical Decision Support Tool on Racial and Ethnic Differences in STI Testing in a Pediatric Emergency Department
April 27
11:04-11:16 a.m.
Josepheen De Asis-Cruz Imaging the Developing Brain: Uncovering the Effects of Prenatal Opioid Exposure
April 27
1:00-2:30 p.m.
Gabrina Dixon The POWER of WORDS – Unconscious Ink Shaping the Careers!
April 27
1:00-2:30 p.m.
Alexandra Corley APA Combined SIG Part 1: Developmental-Behavioral Pediatrics and Race in Medicine
April 27
2:45-3:07 p.m.
Kristen Sgambat Nurturing the Kidney: Updates to CKD Nutritional Guidelines
April 27

2:45-4:15 p.m.

Amanda Stewart Just-in-Time Advocacy: Introducing a Practical, Patient-Centered Framework to Teach Bedside Advocacy
April 27
2:45-4:15 p.m.
Alexandra Corley APA Combined SIG Part 2: Developmental-Behavioral Pediatrics and Race in Medicine

 

Advancing psychological readiness for transformative sickle cell therapies

Dana Footer, PsyD, and Steven Hardy, PhD

Steven Hardy, PhD (left) and Dana Footer, PsyD (right), present Children’s National Hospital’s protocol for assessing psychological readiness for HSCT and gene therapy in sickle cell disease at the European Society for Blood and Marrow Transplantation (EBMT) Annual Meeting.

Hematopoietic stem cell transplant (HSCT) and gene therapy are changing the treatment landscape for sickle cell disease, offering the potential to reduce pain, prevent organ damage and improve quality of life. Alongside these clinical advances, it is essential to ensure patients and families are prepared for these transformative therapies from a psychological and social standpoint.

At Children’s National Hospital, psychologists have developed a structured approach to evaluating and supporting psychosocial readiness for HSCT and gene therapy. This includes addressing mental health concerns, fostering realistic expectations, considering motivations and activating social support networks. Ongoing monitoring after treatment helps ensure patients’ long-term psychological well-being.

This work was recently presented by Dana Footer, PsyD, and Steven Hardy, PhD, at the annual meeting of the European Society for Blood and Marrow Transplantation (EBMT) as an abstract titled A Protocol for Assessing Psychological Readiness for Hematopoietic Stem Cell Transplant and Gene Therapy in Sickle Cell Disease, highlighting Children’s National Hospital’s international leadership in integrating psychosocial care with cell and gene therapies.

Treating the whole patient

During the conference, the Children’s National psychologists within the Cancer and Blood Disorders Center provided concrete recommendations on how to evaluate readiness and use those results to guide individualized, team-based interventions, ensuring patients and families are fully supported throughout the treatment journey.

co-author of the abstract.

This approach helps promote the patient voice, build confidence, strengthen disease self-management, and improve physical and psychosocial outcomes, ensuring care goes beyond treating the disease to supporting the whole person.

Patient and family feedback and real-world experiences continue to inform refinement of the readiness evaluations and interventions. “By  listening to families who have undergone treatment talk about what they found most valuable about the preparation process and which aspects of treatment were surprising to them, we continue learning how best to support future patients,” said Dr. Footer, co-author and attending psychologist in the Divisions of Hematology, Oncology, and BMT.

Leading the field

Access to pediatric HSCT and gene therapy remains limited in the U.S., but Children’s National is a national leader. The embedded psychosocial care providers offer specialized mental health care before, during and after treatment.

By combining clinical innovation with psychosocial expertise, Children’s National is helping ensure these therapies improve not only health outcomes but also patients’ quality of life and ability to pursue their personal goals at every stage of life.

Cardiac surgery team brings pediatric cardiac surgery innovation and research to STS Annual Meeting

A presentation at at the 62nd Society of Thoracic Surgeons (STS) Annual MeetingThe division of pediatric cardiac surgery at Children’s National Hospital had a record number of oral and poster presentations at the 62nd Society of Thoracic Surgeons (STS) Annual Meeting. The STS Annual Meeting is one of the most preeminent education events for both adult and pediatric cardiothoracic surgery.

Children’s National presentations:

Posters

  • Outcomes of Ross Procedure using Freestanding Technique versus Ross Inclusion Technique: A Single Surgeon Experience, Yves d’Udekem, MD, PhD
  • After the Lateral Tunnel Fontan, the Intra-atrial Channel Grows and Remains Pulsatile, Expanding in Systole, Muhammed Ikbal Aydin, MD
  • Tricuspid Valve Repair with Annular Base Patch Leaflet Augmentation in Congenital Cardiac Surgery, Muhammed Ikbal Aydin, MD
  • Recurrence Risk in Subaortic Stenosis: A Comparative Study of Primary and Secondary Lesions, Aybala Tongut, MD
  • Incomplete AVSD: Subtype-Specific Risk Factors and Outcomes Over Two Decades, Aybala Tongut, MD
  • Unroofing Versus Reimplantation Surgical Techniques for Anomalous Aortic Origin of Coronary Arteries Yield Similar Outcomes, Manan Desai, MD
  • Implementation of Elective Exit Angiography after Pediatric Repair of Anomalous Aortic Origin of the Coronary Artery, Manan Desai, MD

Oral abstracts A presentation at at the 62nd Society of Thoracic Surgeons (STS) Annual Meeting

  • Longitudinal Assessment of Laryngeal Ultrasound for Vocal Fold Screening in Pediatrics Post Cardiothoracic Surgery, Lauren Praiss
  • Vocal Cord Palsy in Neonates and Infants after Cardiac Surgery Carries Significant Burden of Care, Aybala Tongut, MD
  • Relationship between Timing of Surgery and Procedure-Specific Outcomes in Neonatal Congenital Heart Surgery, Syed Bukhari, MD
  • Comparative Study of Long-term Outcomes in Infants Undergoing RVOT Reconstruction using Femoral Vein, Pulmonary and Aortic Homograft Conduits, Manan Desai, MD
  • Salvage Left Main Coronary Artery Reimplantation During Arterial Switch Operation, Muhammed Ikbal Aydin, MD

The society’s meeting theme, Teaching for Tomorrow Together, celebrated STS’s dedication to innovation, training the next generation and moving the specialty forward through collaboration and community. This theme aligns closely with the collaborative approach to clinical care, research and education embraced by the Children’s National Heart and Lung Center, leading to the launch of a pediatric cardiac research hub called the Heart Research Institute at Children’s National Hospital.

Children’s National at PES 2026 and a look back at conference research presentations in 2025

Children's National poster presentationThe Children’s National Division of Endocrinology and Diabetes is excited to have 13 posters and presentations at the upcoming Pediatric Endocrine Society (PES) annual meeting in San Francisco, California. The range of topics being presented reflects the breadth of research happening within the division. Many of the posters and presentations continue diving deeper into research presented at conferences across the globe last year. (below)

Poster sessions at PES 2026

  • A Newly Identified Extracellular TSHR Variant and Early-Onset Non-Autoimmune Hyperthyroidism: Two Pediatric Case Reports, Christina Lee, Rachel LongendykeRebecca W. Persky
  • Continuous Glucose Monitor Trends in Children with Glucokinase Maturity-Onset Diabetes of the Young (GCK-MODY), Nicole Rangos, Chaitanya Sambangi, Abby Meyers
  • Qualitative Interviews with Caregivers and Patients with Selected Genetic Causes of Short Stature, Raheem Seaforth, Niusha Shafaei, Kim Pitner, Roopa Shankar, Andrew Dauber
  • Clinical Spectrum of a New Overgrowth Syndrome Due To SPIN4 Dysfunction, Ruta Navardauskaite, Sujin Park … Youn Hee Jee
  • Bone Age Anomalies as Diagnostic Markers of Genetic Growth Disorders, Ruta Navardauskaite, Min Jae Kang, … Hiroki Morizono, Dongkyu Kim, Andrew Dauber, Youn Hee Jee
  • Vosoritide Treatment Improves Linear Growth and Absolute Bone Content and Density in Children with Hypochondroplasia: A 12-Month Prospective Study, … Ruta Navardauskaite, Anqing Zhang, Niusha Shafaei, Raheem Seaforth, Andrew Dauber
  • Vosoritide for Short Stature in Turner Syndrome: Interim results from a Prospective Single Center Trial, Roopa Shankar, Niusha Shafaei, Anqing Zhang, Niti Dham, Kim Pitner, Andrew Dauber
  • Lymphocytic Hypophysitis In An 8-Year-Old With De Novo Deletion at Chromosome 3Q13.31, Christina Lee, Chelsi Flippo
  • WNT/β-CATENIN Modulation by an Epigenetic Reader Gene, SPIN4, Sujin Park, Daniel Li, Yi-Wen Chen, Youn Hee Jee

Oral Abstract Sessions at PES 2026

Children's National at a conference

  • Glycemic Variability and Arterial Stiffness in Youth-Onset Type 2 Diabetes: Interim Analysis of the Young at Heart Study, Nicole Rangos, Elizabeth Estrada, Stephanie Chung
  • A Phase 2 Basket Trial of Vosoritide in Children with Rasopathies, Acan and Npr2 Deficiency, Andrew Dauber, Anqing Zhang, Niusha Shafaei, Raheem Seaforth, Kim Pitner, Niti Dham, Roopa Shankar

Symposium Speakers at PES 2026

  • Meet the Professor: Challenging Thyroid Cases, Priya Vaidyanathan
  • Navigating the Efficacy, Safety and Ethical implications of GLP-1 and SGLT-2 Therapies in Childhood Obesity and Type 2 Diabetes, Elizabeth Estrada

Other notable recent research from the division includes a new international guideline for genetic testing in children with short stature and how vosoritide affects growth signaling in patients with hypochondroplasia.

Below are the posters and presentations from members of our team at conferences last year. We’re excited for another year of research and collaboration with colleagues across the country and globe to improve the lives of children!

European Society of Pediatric Endocrinology

May 10-13, 2025, Copenhagen, Denmark

Invited Symposium Speaker

  • Molecular Basis of Short Stature, Andrew Dauber
  • The evolving diagnostic landscape of hypochondroplasia, Andrew Dauber (Sponsored by BridgeBio)

PES: Pediatric Endocrine Society

May 15-18, 2025, National Harbor, MD

Special Interest Groups/ Presentations

  • A Provider’s Guide to Handling Weight Stigma and Body Image Concerns when Treating Youth with Type 1 and Type 2 Diabetes, Eleanor Mackey
  • Prenatal DSD diagnosis: What Does a Pediatric Endocrinologist Need to Know, *Tucker Pyle

PostersChildren's National poster presentation

European Society of Human Genetics

May 24-27, 2025, Milan, Italy

Invited Symposium Speaker

  • Novel Therapies for Growth Disorders: What Can We Expect from Personalised Medicine, Andrew Dauber

American Diabetes Association

June 20-23, 2025, Chicago, IL
Children's National at a conference
Oral Presentations

Poster Presentations

Latin American Society for Pediatric Endocrinology (SLEP) Annual Meeting

August 6-9, 2025, Panama City, Panama

Invited Symposium Speaker Children's National poster presentation

  • Novel Therapies for Growth Disorders, Andrew Dauber
  • Clinical Predictors of Response to Growth Hormone in Idiopathic Short Stature, Andrew Dauber
  • A Pediatric Endocrinologist’s Guide to the Genetics of Growth, Andrew Dauber
  • Defects in PAPP-A2 Function: From Bedside to Bench and Back Again, Andrew Dauber

The 6th Pediatric Update Conference

September 25-26, 2025, Cairo, Egypt (delivered virtually)

Invited Symposium Speaker

Universidad San Francisco de Quito 4th biennial meeting

October 22-23, 2025, Quito, Ecuador

Invited Symposium Speaker

IPSAD: International Society for Pediatric and Adolescent Diabetes

November 5-8, 2025, Montreal, Canada

Posters without oral presentation

Posters with oral presentationChildren's National poster presentation

2025 T1DX-QI Learning Session

November 11-12, Atlanta GA

Poster Presentation

Oral Presentation

Session Chair

  • Health Equity and Social Determinants of Diabetes, Shideh Majidi

Panel Speaker

Evolving curative therapies for pediatric non-malignant disorders

Children’s National team at the Kuwait Pediatric Stem Cell Transplant, Cellular & Gene Therapy Conference

The Children’s National team at the Kuwait Pediatric Stem Cell Transplant, Cellular & Gene Therapy Conference.

At the Kuwait Pediatric Stem Cell Transplant, Cellular & Gene Therapy Conference, David A. Jacobsohn, MD, MBA, chief of Blood and Marrow Transplantation at Children’s National Hospital, presented emerging approaches that are transforming the treatment of non-malignant pediatric diseases through allogeneic hematopoietic stem cell transplantation (HSCT). His presentation, Pediatric Stem Cell Transplant in Non-Malignant Disorders: Evolving Trends, highlighted sickle cell disease (SCD) as a key example of this progress, noting that decades of advances have made HSCT a highly effective curative option, with survival rates now exceeding 95% for children receiving matched sibling donor transplants. Newer reduced-intensity and non-myeloablative approaches are further lowering treatment-related toxicity while maintaining disease control, significantly decreasing hospitalization burden and improving quality of life.

The talk also addressed one of the field’s most pressing challenges, donor availability, and how the expansion of haploidentical (half-matched) donor strategies is opening curative treatment options to the vast majority of patients who previously lacked a suitable donor. In parallel, evolving conditioning regimens and immune-modulating therapies are helping reduce graft rejection and improve long-term outcomes.

Beyond SCD, the presentation highlighted national and international research efforts demonstrating the curative potential of HSCT for inherited immune disorders such as severe combined immunodeficiency (SCID) and chronic granulomatous disease (CGD). Data from large, multi-center collaborations show that earlier referral, tailored conditioning, and close collaboration between immunology and transplant teams are critical to optimizing survival and immune recovery.

Together, this work underscores a broader shift in pediatric transplantation, moving from high-risk rescue therapy to a more precise, accessible and patient-centered cure. It reinforces the role Children’s National plays in advancing innovative, life-changing treatments for children worldwide.

Children’s National Hospital to host 36th Annual Pediatric Neurology Update

Abstract head silhouette with a glowing geometric brain and blue electric lines, representing neural activity.The Divisions of Neurology and Neurosurgery at Children’s National Hospital are proud to host the 36th Annual Pediatric Neurology Update course. The focus will be on innovations in disorders of intracranial pressure and head pain.

Chairs:

  • Robert Keating, MD, Interim SVP, Neuroscience and Behavioral Medicine Center and Chief, Neurosurgery
  • Marc DiSabella, DO, Associate Chief, Neurology Operations and Director, Headache Program

The course attracts a national audience and brings together neuroscience clinicians and pediatricians in the Washington, D.C. and Mid-Atlantic region.

Guest speakers include:

  • Robert Avery, DO, pediatric neuro-ophthalmologist from Children’s Hospital of Philadelphia
  • Shawn Aylward, MD, pediatric neurologist from Nationwide Children’s Hospital
  • Abhaya Kulkarni, MD, PhD, professor of neurosurgery from Hospital for Sick Children, Toronto.

This year’s course highlights 4 major areas:

  • Primary and Secondary Disorders of Intracranial Pressure
  • Advances in Intracranial Pressure Monitoring
  • Neurodevelopmental, Psychiatric and Rehabilitation Needs of Patients Recovering from Disorders of Intracranial Pressure
  • Hydrocephalus and Current Approaches

We invite you to join us for presentations from experts in the field during this full-day, CME-accredited event on April 16, 2026. This is a hybrid event that will be held virtually and in-person at the Children’s National Research & Innovation Campus.

For more information and to register, visit ChildrensNational.org/NeurologyUpdate.

Shaping the future of epilepsy care: highlights from AES 2025

In early December, several doctors, fellows and faculty from the division of Neurology at Children’s National Hospital attended the American Epilepsy Society (AES) Annual Meeting in Atlanta, Georgia.

This meeting unites a global community of child and pediatric neurologists, neurosurgeons, psychiatrists, neuropsychologists, psychologists, basic translational and clinical scientists, advanced practice providers, advocates and industry professionals to share scientific breakthroughs, foster collaboration and improve outcomes for people living with epilepsy.

Children’s National experts were featured throughout the program, presenting on a wide range of topics in pediatric epilepsy.

Sessions and Workshops

  • Chima Oluigbo, MD: Epilepsy Surgery Skills Workshop | Overcoming Complications in Epilepsy Surgery
  • Dana Harrar, MD, PhD: Resident EEG Course
  • Hua Xie, PhD: Neuroimaging platform | Thalamo-lesional Connectivity Profile Predicting Focal to Bilateral Tonic-Clonic Seizures in Focal Cortical Dysplasia-related Epilepsy
  • John Schreiber, MD: Investigators Workshop | Mortality in DEEs Across the Lifespan: Timing, Causes and Prevention
  • Leigh Sepeta, PhD: Investigators Workshop | Hippocampal Long Axis Differentiation in Memory and Seizure Networks
  • Sara Preisendanz, MS, RD, CSP, LD: Professional Development | Career Pathways: Interprofessional Panel
  • Syed Anwar, PhD, MS: Pediatric State of the Art Symposium | Pediatric Epilepsy Surgery: It’s Not Just About Resection

Poster Presentations

To learn more about the meeting, visit the AES website for additional information.

The best of 2025 from Innovation District

2025 with a lightbulb instead of a zero

In 2025, Innovation District readers gravitated toward stories that explored how research and clinical innovation are reshaping pediatric care in real time. This year’s most popular articles highlighted advances in complex surgical care, evidence-based treatments for chronic and neuropsychiatric conditions and emerging technologies — from wearable data to artificial intelligence — that are changing how clinicians diagnose, treat and support children and families. Read on for our list of the most popular articles we published on Innovation District in 2025.

1. Life-changing care: How Children’s National tackles pediatric cervical spine injuries

The Cervical Spine program at Children’s National Hospital is responsible for treating a range of conditions, including trauma, congenital abnormalities and tumors. These conditions can lead to instability or misalignment of the cervical spine. “There are unique challenges in pediatric cases due to anatomical differences. The cervical spines of children are more at risk for injury because of their developmental stage and structural characteristics,” says Matthew Oetgen, MD, MBA, chief of Orthopaedic Surgery and Sports Medicine at Children’s National.
(2 min. read)

2. Pioneering evidence-based treatments for substance addictions

Increasing evidence-based treatment is a key component of the Addictions Program at Children’s National Hospital, created in 2022 and led by Sivabalaji Kaliamurthy, MD. “We really want to focus on intervening in an evidence-based manner in the primary care setting because that is where most of our patients are going to first access care outside of the emergency room,” explains Dr. Kaliamurthy.
(3 min. read)

3. Breaking barriers in growth disorder treatment for families

For many children with short stature and other rare genetic growth disorders, there have been no next steps after usual treatment options prove ineffective. Researchers at Children’s National Hospital are digging deeper to find the root genetic causes of short stature disorders and creating novel, nuanced treatment options that have the opportunity to change how the field approaches these cases.
(4 min. read)

4. The link between metabolic acidosis and cardiovascular disease in children with CKD

Denver D. Brown, MD, nephrologist at Children’s National, is looking at whether untreated metabolic acidosis could potentially contribute to cardiovascular outcomes in children with chronic kidney disease (CKD). Here, she explains her motivation, findings and future directions for this critical research.
(3 min. read)

5. Therapy approach shows promise for PANS/PANDAS

A multidisciplinary therapy model developed at Children’s National shows promise for children with PANS and PANDAS, significantly reducing symptoms through structured cognitive-behavioral therapy and family-centered care. The approach could offer a new standard for treating these rare, complex neuropsychiatric disorders.
(2 min. read)

6. Wearable tech data shows promise in ADHD detection

A study from Children’s National reveals that common wearable devices like Fitbits may hold the key to improving how we identify Attention-Deficit/Hyperactivity Disorder (ADHD) in adolescents. By analyzing patterns in heart rate, activity levels and energy expenditure, researchers were able to predict ADHD diagnoses with striking accuracy, offering a glimpse into a future where objective, real-time data supports earlier and more personalized mental healthcare.
(2 min. read)

7. Novel pediatric pacemaker shows safety, effectiveness for fragile infants in multi-center study

A novel implantable pacemaker designed specifically for infants has demonstrated safety and effectiveness in stabilizing heart rhythms for at least two years. The multi-center study of 29 infants showed stable pacing, normal electrical parameters and expected battery life, offering a viable alternative to standard-size devices for the smallest children.
(2 min. read)

8. Socioeconomic disadvantage associated with higher long-term mortality for children after heart surgery

Children who had heart surgery and come from less advantaged neighborhoods in the Washington, D.C., region are much more likely to die in the long term than those from neighborhoods with more wealth and opportunity. The finding was part of a presentation titled, Socioeconomic Disadvantage Is Associated with Higher Long-Term Mortality After Cardiac Surgery, by Jennifer Klein, MD, MPH, cardiologist at Children’s National Hospital, during the Society of Thoracic Surgeons Annual Meeting in Los Angeles.
(2 min. read)

9. Children’s National brings AI into the RHD early diagnosis equation

Experts from Children’s National traveled to Uganda to continue work on a pilot program applying artificial intelligence (AI) to the diagnosis of rheumatic heart disease (RHD). The team created a tool that uses AI to predict RHD by identifying leaky heart valves on handheld ultrasound devices, then prompts a referral for a full echocardiogram.
(2 min. read)

10. Fighting food insecurity with fresh produce and education

Food insecurity is rising in Washington, D.C. and it’s hitting families with children the hardest. That’s why Children’s National Hospital created the Family Lifestyle Program (FLiP) – a multi-layered intervention, which offers Patient Navigation (FLiP-PN) and a Produce Prescription Intervention (FLiPRx). FLiP is a Food Is Medicine, clinical-community initiative that helps families get access to fresh food, build healthy habits and lower their risk of diet-related diseases like diabetes and obesity.
(3 min. read)

Showcasing global expertise: Children’s National at the 2025 Pediatric Neuroscience Conference in Qatar

Dr. Elizabeth Wells presenting at the 2025 Pediatric Neuroscience Conference.

Dr. Elizabeth Wells presenting at the 2025 Pediatric Neuroscience Conference.

In early November, experts from the Neuroscience and Behavioral Medicine Center at Children’s National Hospital traveled to Doha, Qatar, to participate in the 5th Annual Pediatric Neuroscience Conference, presented by Sidra Medicine. This marks the second year of partnership between Children’s National and Sidra Medicine for this premier international event.

The annual conference brings together leading clinicians, researchers and innovators from across Neurology, Neurosurgery, Neuro-critical Care, Neurogenetics and Neuroradiology to share the latest insights driving the future of pediatric neuroscience. This year’s program explored the epidemiology and mechanisms of neurological diseases, cutting-edge clinical trials, AI innovations and new models of integrated, high-impact care.

Elizabeth Wells, MD, senior vice president of the Neuroscience and Behavioral Medicine Center at Children’s National and a member of the conference’s Scientific Committee, highlighted the continued impact of this international partnership. “By training and supporting physicians and allied health staff across the region, we’re expanding access to quality care close to home,” said Dr. Wells. “But when children require complex interventions or innovative treatments that aren’t available locally, Children’s National is ready to provide that next level of care. We’re proud to serve both as a partner in strengthening regional capacity and as a global leader in the most advanced pediatric neuroscience therapies.”

“It was a great pleasure to partner once again with Children’s National for this year’s Pediatric Neuroscience Conference,” said Ruba Benini, FRCPSC, MD, PhD, medical director of the Neurodiagnostic Laboratory at Sidra Medicine. “Their high-caliber speakers and the depth of experience they brought to the conference added tremendous value, and we look forward to continuing our collaboration in the future.”

Children’s National brought the largest contingent of external speakers to this year’s meeting, presenting across multiple high-visibility sessions:

Scientific Sessions & Presentations

SESSION II: Neuro-Immunology

Drs. William D. Gaillard, Adelaide Robb and Karen Smith at the 2025 Pediatric Neuroscience Conference.

Drs. William D. Gaillard, Adelaide Robb and Karen Smith at the 2025 Pediatric Neuroscience Conference.

  • Elizabeth Wells, MD — Autoimmune Encephalitis – Updates on Diagnosis & Treatment

SESSION III: Neuro-Oncology

  • Elizabeth Wells, MD — Session Moderator
  • Robert Keating, MDLatest Advances in Non-Invasive Focused Ultrasound Treatment for Brain Tumors

SESSION IV: Neurogenetics and Precision Medicine in Neurological Disorders

  • Sarah Wright, MD Progress and Innovations in Clinical Trials for Neuromuscular Diseases
  • William D. Gaillard, MD Developments in Epilepsy Clinical Trials: Emerging Therapies and Technologies

SESSION V: Epilepsy Symposium

  • William D. Gaillard, MD — Epilepsy Surgery: Patient Selection, Evaluation and Outcomes
  • Chima Oluigbo, MDAdvances in Epilepsy Surgery: Options and Procedures
  • Adelaide Robb, MD Neuropsychiatric Co-Morbidities in Pediatric Epilepsy

SESSION VI: Complex Neurosurgical Procedures

  • Robert Keating, MD — Two Decades of Experience With Chiari Malformations: Where Are We Today?

SESSION VII: Artificial Intelligence and Cutting-Edge Research in Neuroscience

  • Chima Oluigbo, MD — Artificial Intelligence in Neurosurgery: Transforming Diagnosis, Treatment, and Patient Outcomes

Following the conference, Dr. Adelaide Robb and Dr. William D. Gaillard presented Grand Rounds for the psychiatry and neurology departments at Sidra Medicine, further strengthening the educational and clinical collaboration between institutions.

“Our work in the Gulf is rooted in a simple belief: every child deserves access to cutting-edge care and the hope it brings,” says Karen Smith, MD, executive medical director of Global Services at Children’s National. “By partnering with hospitals and government leaders across the region, we’re not only sharing expertise—we’re building sustainable systems that empower communities and transform outcomes for children for years to come.”

To learn more about the Pediatric Neuroscience Conference, visit the conference website.

Global leaders in pediatric neuroscience, including experts from Children’s National, gather at the 2025 Pediatric Neuroscience Conference in Qatar.

Global leaders in pediatric neuroscience, including experts from Children’s National, gather at the 2025 Pediatric Neuroscience Conference in Qatar.

Building the future of pediatric preparedness: Inside SPARK Capstone 2025

Founders from the 2025 SPARK cohort

Founders from the 2025 SPARK cohort take the stage at Capstone and Pitch Day at Children’s National, presenting pediatric-first solutions to national preparedness challenges.

On November 18, the SPARK Hub for Innovations in Pediatrics welcomed federal partners, researchers, clinicians and startup founders to the 2025 Capstone and Pitch Day at the Children’s National Research & Innovation Campus. The event highlighted how pediatric-first innovation strengthens national preparedness and demonstrated the power of coordinated partnerships across the Biomedical Advanced Research and Development Authority (BARDA), the Pediatric Pandemic Network, Children’s National Hospital and the broader venture community.

From diagnostics and vaccines to emergency medicine and clinical devices, this year’s cohort elevated solutions designed to meet children where current systems fall short.

The big picture

The afternoon opened with welcoming remarks from SPARK Principal Investigator Julia Finkel, MD, followed by an overview from BARDA Program Manager Mary Larkin on how federal innovation pathways can accelerate pediatric-focused medical countermeasures.

Her remarks framed the accelerator as part of a larger national strategy: flexible public-private partnerships, non-dilutive funding models and rapid technology development cycles aimed at improving preparedness for infectious disease threats, chemical and radiological hazards and emerging public health emergencies. These same themes carried through the pitches that followed, underscoring how innovation must be timely, evidence-driven and scalable.

Why it matters

A major focal point of the afternoon was the panel discussion, “Ensuring Pediatric Equity in Medical Countermeasures: From Evidence to Action,” featuring BARDA Clinical Development Director Bill Kapogiannis, MD, and Children’s National Chief of Emergency Medicine Joelle Simpson, MD.

The conversation centered on a recurring challenge: children remain underrepresented across the entire lifecycle, including preclinical testing, adaptive trial design, regulatory pathways and distribution strategies. Because children experience distinct physiologic, developmental and social factors during emergencies, any gaps in preparedness amplify disparities.

Panelists emphasized:

  • The need for earlier inclusion of pediatric data in national biodefense strategies
  • System-level reforms to ensure equitable access to countermeasures
  • Stronger partnerships between hospitals, federal agencies and community organizations
  • Lessons from COVID that still have not been fully institutionalized, particularly around surge capacity and supply chain resilience

Their perspective shaped the lens through which the SPARK pitches were viewed: Not simply as emerging technologies, but as essential tools for equity.

Portfolio highlights

SPARK Capstone and Pitch Day 2025 signage

SPARK Capstone and Pitch Day 2025 signage greets partners, founders and clinicians as they gather to advance pediatric preparedness.

The 2025 SPARK cohort tackled some of the most persistent and high-stakes gaps in pediatric preparedness and care.

  • AcQumen Medical: A noninvasive hemodynamic monitoring platform that supports earlier detection of circulatory collapse, sepsis and shock in pediatric intensive care units. By combining ultrasound and impedance technologies, the UltraTrac device delivers accurate, continuous measurements without invasive lines.
  • BugSee: A rapid, same-day diagnostic approach for pediatric sepsis that bypasses slow culture-based workflows. Their selective lysis technology preserves viable bacteria from whole blood, enabling species ID and antibiotic susceptibility testing within hours.
  • Congruence Medical Solutions: A dose-metered delivery platform that allows pegfilgrastim to be safely administered to children at precise microliter quantities. Although the drug is approved for pediatric use, current adult-focused devices prevent accurate dosing.
  • Deep Breathe: A universal lung assessment tool designed for both children and adults, supporting earlier triage, telehealth use cases and improved respiratory decision-making across care settings.
  • Rhinomed: A pediatric-specific nasal swab that significantly reduces testing-related distress, increasing parental willingness to test children for respiratory infections. Its design integrates with existing antigen and PCR platforms and improves comfort without sacrificing accuracy.
  • VaxSyna: A next-generation, antibody-based vaccine platform with multi-antigen display and no adjuvant requirement. Their lead indication targets herpes simplex virus, aiming to address a condition with major neonatal morbidity and no approved vaccine.
  • WearableDose: A real-time absorbed radiation dosimeter delivered as a skin patch. It provides precise, patient-specific measurements, addressing a long-standing gap in pediatric imaging and radiation safety.
  • Vesynta: A pediatrics-first precision dosing digital marketplace that provides clinicians with personalized treatment insights to optimize therapeutic safety and efficacy.
  • Sibel Health: An advanced wearable sensor-based platform for remote pediatric patient monitoring in the context of pandemic response.

What’s next

Following the pitch session, a Fireside Chat session brought together SPARK founders and BioHealth Innovation mentors to explore what comes after the accelerator. They discussed regulatory strategy, commercialization planning and the translational challenges unique to pediatric-focused technologies.

Looking ahead, the SPARK program will continue to guide each company through clinical validation, FDA pathways, BARDA engagement and partnership development. Many are pursuing active or future pilots with Children’s National, strengthening a pipeline of solutions that are grounded in real patient needs and real-world clinical environments.

More broadly, the 2025 cohort reinforces a central theme: Pediatric innovation is essential to national health security. When children are fully integrated into preparedness strategies, the entire healthcare system becomes more resilient, equitable and future-ready.

Advancing pediatric GI care: Children’s National at the 2025 NASPGHAN Conference

A poster session at the 2025 NASPGHAN ConferenceIn early November, doctors, fellows and faculty from the division of Gastroenterology, Hepatology and Nutrition at Children’s National Hospital attended the North American Society for Pediatric Gastroenterology, Hepatology and Nutrition (NASPGHAN) conference in Chicago.

The annual conference brings together experts from across the nation to discuss and learn about normal pediatric development and how pediatric gastrointestinal, liver and nutritional disorders can disrupt it.

Presenters and topics from Children’s National included:

Receptions & Concurrent Sessions

  • Diana Moya, MD, program director: Fellowship program reception
  • Ian Leibowitz, MD: Show Me the Money! Unlocking Your Financial Potential. Mastering the Negotiation Game – Tactics for Success.

Poster Presentations

  • Diana Jo, MD, Nathan Bryan, DO, Christopher Hayes, MD: Just around the bend: An elusive case of dysphagia lusoria in a young boy.
  • Udeme Ekong, MBBS MD, Khalid Khan, MD, Kimberly Chapman, MD, Carolina Rumbo, MD, Nada Yazigi, MD: Long term risk for metabolic syndrome in pediatric liver transplant recipients with metabolic disorders: A retrospective clinical chart review.
  • Brenna Hohl, DO, Migseg Sanchez, DO, Diana Moya, MD: Bronchiolitis obliterans organizing pneumonia in a pediatric patient with Crohn’s disease: A rare extra-intestinal manifestation.
  • Catherine Raber, Shayna Coburn, PhD: Feasibility and acceptability of routine weekly at-home gluten immunogenic peptide testing in teens in a 6-week behavioral intervention for celiac disease.
  • Catherine Raber, Vahe Badalyan, MD: Clinical outcomes of children with potential celiac disease in North America: A multicenter retrospective study.
  • Christopher Hayes, MD: Therapeutic trial of Sucraid® (sacrosidase) for alleviating gastrointestinal symptoms in pediatric subjects stratified by duodenal sucrase activity levels.
  • Migseg Sanchez, DO, Jyoti Mani, MD: Occult esophageal foreign body identified during evaluation of chronic vomiting in a toddler.
  • Serena Haver, MD, Diana Jo, MD, Otto Louis-Jacques, MD: Evaluating the impact of swallowed topical steroids on growth in children with eosinophilic esophagitis.
  • Nathan Bryan, DO, Kibileri Williams, MBBS, Diana Moya, MD, Christopher Hayes, MD: Predictors for readmission in newly diagnosed pediatric inflammatory bowel disease.
  • Vahe Badalyan, MD, Clarivet Torres, MD: Management of small intestinal bacterial overgrowth (SIBO) in pediatric short bowel syndrome (SBS).
  • Joi McLaughlin, MD, Christopher Hayes, MD: A rare case of diagnosis and endoscopic reduction of ileocecal intussusception secondary to Burkitt’s lymphoma.
  • Guy Ozigre, Vahe Badalyan, MD: Endoscopic success: avoiding surgery in an autistic child with multiple magnet ingestions.
  • Anil Darbari, MD, Ian Leibowitz, MD, Deepika Darbari, MD, Diana Jo, MD, Nathan Bryan, DO: Management considerations in patients with inflammatory bowel and sickle cell disease.

To learn more about the meeting, explore the NASPGHAN website for additional information.

Children’s National psychiatry experts to present at 2025 AACAP Annual Meeting

2025 American Academy of Child and Adolescent Psychiatry (AACAP) Annual Meeting logoSeveral experts from the Division of Psychiatry and Behavioral Sciences at Children’s National Hospital will showcase their expertise at this year’s American Academy of Child and Adolescent Psychiatry (AACAP) Annual Meeting, taking place October 20–25 in Chicago, Illinois. As the world’s largest gathering of child and adolescent psychiatrists, AACAP provides a forum for sharing research, exchanging knowledge and advancing care for patients worldwide.

Children’s National experts will be featured throughout the program, presenting on a wide range of topics in adolescent psychiatry.

Presentations and sessions

Date Time (CST) Presenter(s) Title
10/20/25 3–5 PM Justine Larson, MD Institute 1: Reclaiming Hope: Strengthening Families Through Systems-of-Care Approaches
10/20/25 3:30–5:30 PM Jennifer Dorr, DO, MPH, Laura M. Willing, MD Clinical Case Conference 3: How Advocacy Work IS Clinical Work: A Clinical Presentation
10/21/25 8:30–11 AM Colby Tyson, MD Member Services Forum 2: The Child and Adolescent Psychiatrist Parent: Navigating Family Planning, Parental Leave, and Early Parenthood
10/21/25 1–3 PM Justine Larson, MD Clinical Case Conference 6: Navigating the Storm: A Multidisciplinary Approach to Mood and Behavior Dysregulation in Adolescents
10/22/25 12–2 PM Adelaide S. Robb, MD Institute 4.6: Grading the Evidence – Bipolar Disorder and Schizophrenia
10/23/25 7–8:30 AM Justine Larson, MD Clinical Consultation Breakfast 4: Anxiety in Adolescents With ASD
10/23/25 7–8:30 AM Sivabalaji Kaliamurthy, MD Clinical Consultation Breakfast 8: Engaging Adolescents With Co-Occurring Substance Use and Psychiatric Disorders
10/23/25 9 AM–12 PM Adelaide S. Robb, MD Workshop 21: Understanding Video Games: A Child Psychiatrist’s Call of Duty
10/23/25 10 AM–12 PM Sivabalaji Kaliamurthy, MD Clinical Case Conference 9: Synthetic vs Nonsynthetic Cannabinoid-Induced Psychosis in Adolescents
10/23/25 12–2 PM Adelaide S. Robb, MD Clinical Perspectives 57: Mastering Psychotropic Medication Management in Youth
10/23/25 1:30–4:30 PM Sivabalaji Kaliamurthy, MD Workshop 24: Buprenorphine 2.0
10/23/25 7–10 PM Priya M. Punnoose, MD Media Theatre 11: Faith, Family, and Teen Religious Identity: Are You There God? It’s Me, Margaret
10/24/25 9–11 AM Sivabalaji Kaliamurthy, MD Clinical Perspectives 72.4: Hallucinogen Use Disorder in Adolescents and Transitional-Age Youth
10/24/25 9 AM–12 PM Jennifer Dorr, DO, MPH Hot Air, Hot Water, Hot Topics: Child and Adolescent Psychiatrists Leading the Way Through Chaos
10/24/25 12–2 PM Adelaide S. Robb, MD Debate: Should High Schools Ban Smartphones?
10/24/25 2–4 PM Mahdieh Bodaghi, MD Clinical Case Conference 14: Untangling Disorders of Gut–Brain Interaction With Psychiatric Comorbidities
10/24/25 3–5 PM Justine Larson, MD Institute 8.6: Creating Trauma-Informed Systems of Care
10/25/25 11 AM–12:30 PM Hanife Nur Akal, MD Special Interest Study Group 10: “Healing After Disaster”: Trauma-Informed, Community-Based Interventions

Abstracts

New Research Poster 5.19: Pilot Study of an Integrated Psychiatry Clinic Within a Pediatric Practice
Melissa Kelley, MD
Friday, October 24 – 10:30 AM-12:30 PM

New Research Poster 6.6: Improving Pediatric Trainees’ Management of Common Pediatric Mental and Behavioral Conditions
Geoffrey Broadbent, MD, Katelyn Gerth, MD, Jeannie Chang Pitter, MD
Saturday, October 25 – 10 AM-12 PM

For more information and to view the full schedule, please visit the AACAP conference website.

Looking ahead: Children’s National faculty and fellows prepare for Kidney Week 2025

Kidney Week 2025 logoThis November, doctors, fellows and faculty from the Division of Nephrology at Children’s National Hospital will join more than 12,000 kidney professionals at Kidney Week 2025 in Houston, Texas. Hosted annually by the American Society of Nephrology (ASN), this event offers a unique opportunity for attendees to engage in discussions and collaborations focused on the latest breakthroughs and innovations in nephrology.

Professionals and leaders from Children’s National will play a prominent role throughout the weekend, showcasing their expertise in a variety of sessions and presentations including:

Session Moderators

Poster Presentations

  • Ashley Trinh, MD (Nephrology Fellow): “Granulomatous Tubulointerstitial Nephritis in Pediatric Inflammatory Bowel Disease: A Case Report”
  • Jordy Salcedo-Giraldo, MD (Nephrology Fellow): “A Rare Case of Rapidly Progressive Kidney Failure in Alport Syndrome with Crescents”
  • Jordy Salcedo-Giraldo, Krista Wink, Nicholas Dadzie, Andrew Freiman, MS, CGC & Ashima Gulati, MD, PhD: “Variants of Uncertain Significance Burden Quantification and Reclassification in a Pediatric Kidney Genetics Clinic”
  • Krista Wink, Jordy Salcedo-Giraldo & Ashima Gulati: “Multidisciplinary Care Needs in Children with ADPKD”
  • Krista Wink, Jordy Salcedo-Giraldo, Andrew Freiman, Tucker Pyle, MD, PhD & Ashima Gulati: “The Inherited and Polycystic Kidney Disease Program at Children’s National Hospital”

Additionally, Dr. Denver Brown’s article published in Kidney360, Metabolic Acidosis and Cardiovascular Disease Risk in Children with CKD, has been selected to be presented during the “Best of ASN Journals: JASN, CJASN, and Kidney360″ session.

To view the full schedule with details, visit the ASN website.

REI Week 2025 empowers the future in pediatric research and innovation

Children’s National Hospital hosted its fifteenth annual Research, Education and Innovation Week from March 31–April 4, 2025, bringing together clinicians, scientists, educators and innovators from across the institution to celebrate discovery and collaboration. This year’s theme, “Empowering the Future in Pediatric Research and Innovation with Equity, Technology and a Global Reach,” served as a call to action for advancing science that improves child health both locally and around the world.

Each day of the week-long event featured thought-provoking lectures — now available to watch — dynamic panel discussions, interactive workshops and vibrant poster sessions, all highlighting the diverse and interdisciplinary work taking place across Children’s National.

Centering the patient and the planet

REI Week began on Monday with a powerful keynote lecture from Lynn R. Goldman, MD, MS, MPH, Michael and Lori Milken dean of the Milken Institute School of Public Health at the George Washington University. In her talk, “Children: Uniquely vulnerable to climate-related threats,” Dr. Goldman underscored the urgent need to protect children from the environmental hazards of a changing climate and to integrate climate science into pediatric care and advocacy.

At mid-morning, Mary-Anne “Annie” Hartley, MD, PhD, MPH, director of the LiGHT Laboratory at École Polytechnique Fédérale de Lausanne, introduced the “MOOVE” platform — Massive Open Online Validation and Evaluation of clinical LLMs. Her talk demonstrated how artificial intelligence, when rigorously validated, has the potential to transform clinical decision-making and global health equity.

Monday’s final keynote, “Zinc and childhood diarrhea,” was presented by Christopher Duggan, MD, MPH, director of the Division of Nutrition at Harvard Medical School. Dr. Duggan highlighted the global health impact of zinc supplementation in reducing childhood mortality — a reminder that simple, evidence-based interventions can save millions of lives.

In that first day, the first poster session of the week showcased projects in adolescent medicine, global health, infectious diseases, oncology and more. The session reflected the full breadth of research taking place across Children’s National.

Ambroise Wonkam, MD, PhD, professor of genetic medicine at Johns Hopkins University, then delivered Tuesday’s Global Health Keynote Lecture, “Harnessing our common African genomes to improve health and equity globally.” His work affirmed that inclusive genomics is key to building a healthier world.

Later, the Global Health Initiative event and GCAF Faculty Seminar encouraged attendees to pursue collaborative opportunities at home and abroad, reflecting the growing global footprint of Children’s National research programs.

Transforming education and care delivery

On Wednesday, Larrie Greenberg, MD, professor emeritus of pediatrics, kicked off the day with a Grand Rounds keynote on educational transformation: “Shouldn’t teachers be more collaborative with their learners?” He followed with a CAPE workshop exploring the effectiveness of case-based learning.

The Nursing Sponsored Keynote Lecture by Vincent Guilamo-Ramos, PhD, MPH, LCSW, ANP-BC, PMHNP-BC, FAAN, explored “Redesigning the U.S. broken health system.” He offered an urgent and inspiring call to reimagine pediatric care by addressing social determinants of health.

In the Jill Joseph Grand Rounds Lecture, Deena J. Chisolm, PhD, director of the Center for Child Health Equity at Nationwide Children’s Hospital, challenged attendees to move beyond dialogue into action in her talk, “Health equity: A scream to a whisper?,” reminding researchers and clinicians that advocacy and equity must be foundational to care.

The day continued with a poster session spotlighting medical education, neonatology, urology and neuroscience, among other fields.

Posters and pathways to progress

Throughout the week, poster sessions highlighted cutting-edge work across dozens of pediatric disciplines. These sessions gave attendees the opportunity to engage directly with investigators and reflect on the shared mission of discovery across multiple disciplines, including:

Honoring excellence across Children’s National

The REI Week 2025 Awards Ceremony celebrated outstanding contributions in research, mentorship, education and innovation. The winners in each category were:

POSTER SESSION AWARDS

Basic & Translational Research

Faculty:  Benjamin Liu, PhD

“Genetic Conservation and Diversity of SARS-CoV-2 Envelope Gene Across Variants of Concern”

Faculty:  Steve Hui, PhD
“Brain Metabolites in Neonates of Mothers with COVID-19 Infection During Pregnancy”

Faculty: Raj Shekhar, PhD
“StrepApp: Deep Learning-Based Identification of Group A Streptococcal (GAS) Pharyngitis”

Post docs/Fellows/Residents: Dae-young Kim, PhD
“mhGPT: A Lightweight Domain-Specific Language Model for Mental Health Analysis”

Post docs/Fellows/Residents: Leandros Boukas, MD, PhD
“De Novo Variant Identification From Duo Long-Read Sequencing: Improving Equitable Variant Interpretation for Diverse Family Structures”

Staff: Naseem Maghzian
“Adoptive T Lymphocyte Administration for Chronic Norovirus Treatment in Immunocompromised Hosts (ATLANTIC)”

Graduate Students: Abigail Haffey
“Synergistic Integration of TCR and CAR T Cell Platforms for Enhanced Adoptive Immunotherapy in Brain Tumors”

High School/Undergraduate Students: Medha Pappula
“An ADHD Diagnostic Interface Based on EEG Spectrograms and Deep Learning Techniques”

Clinical Research

Faculty: Folasade Ogunlesi, MD
“Poor Air Quality in Sub-Saharan Africa is Associated with Increase Health Care Utilization for Pain in Sickle Cell   Disease Patients”

Faculty: Ayman Saleh, MD
“Growth Parameters and Treatment Approaches in Pediatric ADHD: Examining Differences Across Race”

Post docs/Fellows/Residents: Nicholas Dimenstein, MD, MPH
“Pre-Exposure Prophylaxis (PrEP) Eligibility in the Pediatric Emergency Department”

Staff: Tayla Smith, MPH
“The Public Health Impact of State-Level Abortion and    Firearm Laws on Health Outcomes”

Graduate Students: Natalie Ewing
“Patterns of Bacteriuria and Antimicrobial Resistance in Patients Presenting for Primary Cloacal Repair: Is Assisted Bladder Emptying Associated with Bacteriuria?”

Graduate Students: Manuela Iglesias, MS
“Exploring the Relationship Between Child Opportunity Index and Bayley-III Scores in Young Children”

High School/Undergraduate Students: Nicholas Lohman
“Preliminary Findings: The Efficacy, Feasibility and Acceptability of Group Videoconference Cognitive Behavioral Therapy with Exposure and Response Prevention for Treating Obsessive-Compulsive Disorder Among Children and Young People”

Community-Based Research

Faculty: Sharon Shih, PhD
“Assessing Pediatric Behavioral Health Access in DC using Secret Shopper Methodology”

Post docs/Fellows/Residents: Georgios Sanidas, MD
“Arrested Neuronal Maturation and Development in the Cerebellum of Preterm Infants”

Staff: Sanam Parwani

“Intersectionality of Gender and Sexuality Diversity in Autistic and Non-Autistic Individuals”

Graduate Student: Margaret Dearey
“Assessing the Burden of Period Poverty for Youth and Adolescents in Washington, DC: A Pilot Study”

Quality and Performance Improvement

Faculty: Nichole L. McCollum, MD
“A Quality Improvement Study to Increase   Nurse Initiated Care from Triage and Improve Timeliness to Care”

Post docs/Fellows/Residents:  Hannah Rodriguez, MD
“Reducing Unnecessary Antibiotic Use in a Level IV NICU”

Staff: Amber K. Shojaie, OTD, OTR/L
“Implementing Dynamic Axilla Splints in a Large Burn Patient”

MENTORSHIP AWARDS

Basic Science Research

Conrad Russell Y. Cruz, MD, PhD

Clinical Research

Rana Hamdy, MD, MPH, MSCE

Bench to Bedside Research

Ioannis Koutroulis, MD, PhD, MBA

ELDA ARCE TEACHING SCHOLAR AWARD

Priti D. Bhansali, MD, MEd

Heather Ann Walsh, PhD, RN

SUZANNE FEETHAM NURSING RESEARCH SUPPORT AWARD

Eileen P. Engh, PhD RN 
“Rare Disease Organization Lifecycle” Role in Helping Parents with Everyday Life Information Seeking and Connection (RDO-HELIX)

EXPLORATIONS IN GLOBAL HEALTH PILOT AWARDS

Launchpad Awards

Mi Ran Shin, MD, MPH
“Establishing Interdisciplinary Rehabilitation for Birth and Burn Injuries in Ethiopia”

Susan Harvey, MSN, CPNP-AC
“Implementation of Sickle Cell Pilot Program in Ndhiwa Sub County, Kenya”

Meleah Boyle, PhD, MPH
“Understanding and Addressing Environmental Sustainability to Protect the Health of the Children’s National and Global Communities”

Eiman Abdulrahman, MD
“Research Capacity Building to Improve Pediatric Emergency and Critical Care in Ethiopia”

Pilot Awards

Alexander Andrews, MD
“EEG as a Diagnostic and Prognostic Marker in Severe Pediatric Malaria, Blantyre Malawi”

Daniel Donoho, MD & Timothy Singer, MD
“Feasibility Study of a Novel Artificial Intelligence-Based Educational Platform to Improve Neurosurgical Operative Skills in Tanzania”

Hasan Syed, MD
“Bridging the Gap an Educational Needs Assessment for Pediatric Neurosurgery Training in Pakistan”

Sofia Perazzo, MD & Lamia Soghier, MD, MEd, MBA
“QI Mentorship to Improve Pediatric Screening and Follow-up in Rural Argentina”

Benjamin Liu, PhD
“AI-Empowered Real-Time Sequencing Assay for Rapid Detection of Schistosomiasis in Senegal”

Rae Mittal, MD
“Assessment and Enhancement of Proficiency in Emergency Child Neurology Topics for Post-Graduate Emergency Medicine Trainees in India”

Innovation Day ignites bold thinking

Thursday, REI Week shifted to the Children’s National Research & Innovation Campus for Innovation Day, a celebration of how bold ideas and collaborative culture can accelerate progress in pediatric medicine.

Brandy Salmon, PhD, associate vice president of Innovation and Partnerships at Virginia Tech, opened the day with “The Alchemy of Innovation,” focusing on how institutions can build a culture that fuels transformative partnerships.

A multidisciplinary panel discussion moderated by Nathan Kuppermann, MD, MPH, and Catherine Bollard, MBChB, MD, featured Nehal Mehta, MD, Julia Finkel, MD, Kevin Cleary, PhD, Ioannis Koutroulis, MD, PhD, MBA, Francesca Joseph, MD and Patrick Hanley, PhD, who shared how innovation can be advanced and promoted, especially as a core institutional priority.

A shared vision for the future

REI Week 2025 reaffirmed the values that define Children’s National: a commitment to excellence, collaboration and equity in pediatric research and care. As discoveries continue to emerge from our hospital and our research campuses, the connections built and ideas sparked during this week will help shape the future of pediatric health — locally and globally.

By elevating voices from the bedside to the bench, with the support of the executive sponsors Nathan Kuppermann, MD, MBChB, Catherine Bollard, MBChB, MD, Kerstin Hildebrandt, MSHS, Linda Talley, MS, RN, NE-BC and David Wessel, MD, REI Week demonstrated that we must embrace the community in all aspects of our work. Because we know that there are answers we can only get from the patients that we serve—and we need to be their voice.

Research, Education & Innovation Week will be back next year on April 13-17, 2026.

Children’s National experts at the 2025 Tandem Meetings

Experts from Children’s National Hospital at the 2025 Tandem Meetings

Nurse Practitioner Sameeya Ahmed-Winston, CPNP, CPHON, was recognized with the APP Lifetime Achievement Award.

Experts from Children’s National Hospital presented and showcased their latest research at the 2025 Tandem Meetings in Hawaii.

This leading global conference on hematopoietic cell transplantation (HCT), cellular therapy and gene therapy brings together top specialists to share groundbreaking discoveries, innovative technologies and the latest scientific advancements shaping the field.

Fellow Henna Butt, MD, won Best Abstract for her research paper – Comparative Analysis of CRISPR-Cas9, Lentiviral Transduction and Base Editing for Sickle Cell Disease Therapy in a Murine Model.

Nurse Practitioner Sameeya Ahmed-Winston, CPNP, CPHON, was recognized with the APP Lifetime Achievement Award.

Additional presenters:

These achievements highlight Children’s National Hospital’s commitment to advancing research and improving treatments for patients with complex conditions. By sharing their expertise on a global stage, these specialists help shape the future of patient care and improve outcomes for children worldwide

Read more highlights from the 2025 Tandem Meetings here.

Children’s National Hospital to host 35th Annual Pediatric Neurology Update

illustration of the brain on black backgroundThe Divisions of Neurology and Neurosurgery at Children’s National Hospital are proud to host the 35th Annual Pediatric Neurology Update course.

Chair Elizabeth Wells, MD; Co-Chairs, Marc DiSabella, DO, John Schreiber, MD, William D. Gaillard, MD, Robert Keating, MD

The course attracts a national audience and brings together neuroscience clinicians and pediatricians in the Washington, D.C. and Mid-Atlantic region.

Guest speakers include Annapurna Poduri, MD, MPH, Deputy Director for NINDS, Emily Freilich, MD, from the FDA and Conor Mallucci, MBBS, Chief of Neurosurgery at Alder Hays, England.

This year’s course highlights 3 major areas:

  • Updates in Epilepsy
  • Innovations in Vascular Neurosurgery and Neurointerventional Radiology
  • Addressing Mental and Behavioral Health in Neurological Conditions

We invite you to join us for presentations from experts in the field during this full-day, CME accredited event on April 10, 2025. This is a hybrid event that will be held virtually or in-person at the Children’s National Research & Innovation Campus.

For more information and to register, visit ChildrensNational.org/NeurologyUpdate.

Advancing epilepsy care: Highlights from the 2024 American Epilepsy Society Conference

Dr. Gaillard, Dr. Schreiber and Dr. Cohen from Children’s National Hospital at the 2024 American Epilepsy Society meeting.

Dr. Gaillard, Dr. Schreiber and Dr. Cohen from Children’s National Hospital at the 2024 American Epilepsy Society meeting.

The 2024 American Epilepsy Society (AES) conference, held over five days, brought together healthcare professionals, scientists and industry leaders from around the globe. This annual event focuses on advancing outcomes for people with epilepsy through educational sessions, cutting-edge research and the latest technological innovations.

Recognized amongst his peers as an international leader in epilepsy research, William D. Gaillard, M.D., was honored with the 2024 Clinical Science Research Award at this year’s meeting. His pioneering work has significantly enhanced our understanding of epilepsy’s impact on brain structure and has led to improvements in surgical interventions and patient outcomes. Dr. Gaillard’s ongoing contributions to enhancing the lives of children with epilepsy earned him the Society’s most prestigious research award.

Dr. Gaillard serves as chief of the Divisions of Child Neurology and of Epilepsy and Neurophysiology, Director of the Comprehensive Pediatric Epilepsy Program and Associate Director of the Center for Neuroscience Research at Children’s National Hospital.

In addition to Dr. Gaillard, experts from the Comprehensive Pediatric Epilepsy Program at Children’s National were invited to present their research, insights and innovations during the conference. As a recognized Level 4 epilepsy center by the National Association of Epilepsy Centers, the program’s collaborative team is recognized worldwide for their leadership in improving the lives of children with epilepsy through personalized care, advanced technology and groundbreaking research.

Highlights from AES 2024 include:

Sanam Zarei, M.D., Children’s National Hospital Neurology fellow, presenting a poster at AES 2024.

Dr. Zarei, Children’s National Hospital Neurology fellow, presenting a poster at AES 2024.

Poster presentations:

  • Asymmetrical Hippocampal-cortical Connectivity Along Lateral-Medial Axis in Pediatric Focal Epilepsy Patients by Hua Xie, Ph.D., Chloe A. Hooker, William D. Gaillard, M.D.
  • Comorbidities and Concerns in Hypothalamic Hamartoma: Results of an International Caregiver Survey by Nathan Cohen, M.D.
  • Automated and Interpretable Detection of Hippocampal Sclerosis in temporal lobe epilepsy: AID-HS by Nathan Cohen, M.D.
  • Characteristics and Outcomes of Pediatric Patients with Prolonged Convulsive Status Epilepticus by William D. Gaillard, M.D.
  • High Accuracy for Detecting Tonic Clonic seizures (TCSs) Using an Apple Watch Seizure Detector by Dewi Depositario-Cabacar, M.D., William Gaillard, M.D.
  • Patient and Pre-surgical Testing Characteristics Contributing to Duration of Evaluation: Identifying Best Practices and Opportunities to Streamline Pediatric Epilepsy Surgery Evaluation by Dewi Depositario-Cabacar, M.D., William Gaillard, M.D.
  • Seizure Burden in Infants with Hemimegaloencephaly pre- and post Staged Transarterial Embolization by Ersida Buraniqi, M.D., Shani Israel, Lindsay Ruffini, CPNP, CPNP-AC, CPNP-PC, Tammy Tsuchida, M.D., Ph.D., Tayyba Anwar, M.D.
  • Acute Postoperative Seizures (APOS) in Pediatric Epilepsy Surgery Occurring Less Than 7 Days versus Greater Than 7 to 30 Days: Is There a Difference in Long Term Outcome? by Sanam Zarei, M.D., Kathryn Havens, PA-C, Nathan Cohen, M.D., John Schreiber, M.D., Thuy-Anh Vu, M.D., William Gaillard, M.D., Dewi Depositario-Cabacar, M.D.

Invited speakers and topics:

  • Speaker: John Schreiber, M.D., Moving Forward: Epilepsies with Concomitant Movement Disorders
  • Speaker: Laura Tochen, M.D., Moving Forward: Epilepsies with Concomitant Movement Disorders
  • Speaker: William Gaillard, M.D., US Health Care Inequities for People with Epilepsy
  • Session Moderator: Nathan Cohen, M.D., Neuroimaging

Learn more about the Comprehensive Pediatric Epilepsy Program at Children’s National Hospital.

Children’s National shares insights at 2024 T1DX-QI Learning Session

the 8th Annual 2024 T1DX-QI logoExperts from Children’s National Hospital presented research at the 8th Annual 2024 T1DX-QI (Type 1 Diabetes Exchange Quality Improvement Collaborative) Learning Session held in Chicago, Ill. This session emphasizes delivering equitable, evidence-based and cost-effective diabetes care through integrating clinical science, quality improvement, technology and advocacy.

Oral Presentations:

  • Assessing Readiness to Transition to Adult Care among Young Adults with T1D by Jody Grundman, M.D.
  • Improving Microalbuminuria Screening Rates Among Pediatric Diabetes Patients: A Clinic-Wide Initiative by Sarah Lydia Holly, BSN, RN.
  • Addressing Disparities in Diabetes Care: Implementing SDOH Screening at Diagnosis by Sarah Lydia Holly, BSN, RN.
  • Developing a Tracking Tool for Insulin Pump Prescriptions Among Children and Adolescents with Type 1 & Type 2 Diabetes by Amanda Perkins, N.P., C.P.N.P., M.P.H.

Learn more about these presentations here.

Regional powerhouse: Cell and Gene therapy leaders from mid-Atlantic forge connections

Nearly 200 biomedical leaders from Washington, D.C., Maryland, and Virginia gathered at the Children’s National Research & Innovation Campus for the 2nd annual Cell & Gene Therapy Symposium. The event showcased groundbreaking developments in rare disease treatments and underscored the importance of regional collaboration.

“By targeting diseases at the cellular level, we are on the cusp of breakthroughs in cell and gene therapy that will transform medicine,” said Catherine Bollard, M.D., M.B.Ch.B., director of the Center for Cancer and Immunology Research (CCIR) at Children’s National Hospital and a host of the symposium. “Progress will accelerate if we build partnerships beyond our own organizations.”

The big picture

Scientists and clinicians have worked for more than two decades to develop cell and gene therapies aimed at treating diseases on a cellular level. The past few years have been particularly promising as investment in science has led to advancements. Children’s National is at the forefront, as one of the first pediatric hospitals in the world to offer commercial gene therapies for sickle cell disease.

Many more treatments for rare diseases are in development at Children’s National and beyond. Leaders at CCIR are actively building collaborations with companies, academic institutions and enterprises across the mid-Atlantic region to accelerate these efforts.

During the symposium, Eugene Hwang, M.D., chief of Oncology at Children’s National, addressed the urgent need for more effective and less toxic treatments for pediatric brain tumors. He highlighted the potential of combining immunotherapies with innovations like low-intensity focused ultrasound, which can open the blood-brain barrier temporarily to improve drug delivery to tumors.

“With collaboration between the lab and clinic, alongside industry partners and even between hospitals, we can finally make strides I haven’t seen in my entire career,” Dr. Hwang said. “It’s an incredibly inspiring time for all of us.”

Why it matters

Experts from organizations as diverse as MaxCyte, ScaleReady, RoosterBio, PSC Biotech, Qiagen, FujiFilm and the Frederick County Office of Economic Development came together for the daylong conversation.

Michael Friedlander, Ph.D., executive director of the Fralin Biomedical Research Institute at Virginia Tech, emphasized the critical role of regional partnerships in fulfilling the potential of these emerging therapies. He pointed to the collaborative research between Children’s National and Virginia Tech on brain tumors, where bioengineers and cancer researchers are working side-by-side to create new treatments.

“We are now able to begin delivering these leading-edge therapies to patients,” Dr. Friedlander said. “For example, those who live in rural settings often have much less access to such frontline medical innovations. By collaborating with Children’s National and gaining access to urban pediatric populations, as well as patients in our more rural area, we can start to bring these therapies to a much broader audience.”

What’s next

Patrick Hanley, Ph.D., chief and director of the Cellular Therapy Program at Children’s National, observed that other regions in the U.S. are uniting to advance scientific discoveries with the backing of government, academia and industry. He hopes to see similar collaboration across the D.C., Maryland, and Virginia area, known as the DMV. Children’s National is leading an initiative called CHARM – the Capital Health and Mid-Atlantic Regenerative Medicine – to bring regional experts together for webinars, networking events and partnership opportunities.

“There’s significant interest in cell and gene therapy worldwide,” said Dr. Hanley, a symposium host. “I see an even greater interest in creating cell and gene therapy hubs. The time is right for our mid-Atlantic region, and I’m excited to see what unfolds in the next five years.”

Advancements in nephrology: Highlights from ASN 2024 Kidney Week

Kidney Week attendees from Children's National HospitalThousands of medical professionals and researchers from around the world gathered in San Diego this October for Kidney Week 2024. The American Society of Nephrology’s (ASN) annual meeting and scientific exposition featured advances in treatment, research and technology in the fight against kidney disease.

Doctors, fellows and faculty from Children’s National Hospital participated, presenting their latest research and clinical advancements in pediatric kidney disease.

Posters and topics from Children’s National included:

  • Jordy Salcedo-Giraldo, M.D., FAAP: Structured Application of Nephrogenetics in a Pediatric Kidney Clinic Is Clinically Impactful and Challenging
  • Jordy Salcedo-Giraldo, M.D., FAAP: Unmasking the Mimickers: HNF1B Variants in Pediatric Kidney Diseases
  • Sarah Rogal, M.D., Ph.D.: Rapidly Progressive Kidney Failure in a Patient with Longstanding Juvenile Dermatomyositis
  • Jennifer Nhan, M.D.: AKI in Patients with Multisystem Inflammatory Syndrome in Children
  • Krista Wink: The Inherited and Polycystic Kidney Disease Program
  • Kaushalendra Amatya, Ph.D.: Barriers to Communication with Transplant Providers Among Pediatric Kidney Transplant Patients and Their Caregivers

Additionally, there was a presentation from Denver Brown, M.D.: Low Serum Bicarbonate and Cardiovascular Disease Risk in Children with CKD.

Learn more about the IPKD program and the division of Nephrology at Children’s National.